A message to the Fragile X community from Dr. Dayno on behalf of the team at Harmony Biosciences:
Representatives from Harmony Biosciences will be attending the 19th International Fragile X Conference with us in Orlando, Florida. They are excited to come together with the Fragile X community to listen, learn, and help pave the way for brighter futures.
If you see a member of the Harmony Biosciences team, don’t hesitate to say “hello” and ask about about their commitment to the Fragile X community and advancing science and treatment options.
learn more
Visit the RECONNECT MyFXReserach post for more infromation:
Clinical Trial RECONNECT: ZYN002 Gel | MyFXResearch Portal (fragilex.org)
Gene therapies in action: a look at examples of successful treatments
Although there are currently no options for approved or experimental gene therapies for FXS, gene therapies in other diseases and conditions do exist and are helping people today! Read the blog to see some examples of gene therapy in the real world!
EXPERIENCE Clinical Trials – Join Today!
You may have heard about EXPERIENCE (Evaluation of Fragile X Experience in Cognition Expression) clinical trials as the Tetra studies or the studies of BPN14770 in Fragile X syndrome. EXPERIENCE is now being managed by Shionogi and clinical trial sites across the U.S. are still enrolling qualified male participants aged 9-45.