Study of MRM-3379 in Male Participants With Fragile X Syndrome (BLOOM)

  • Condition: Fragile X Syndrome
  • Age: Child, Adult 18+
  • Sex: Male

A Phase 2 clinical trial testing the safety and effectiveness of the oral drug MRM-3379 in males with Fragile X syndrome, focusing on potential improvements in cognition, behavior, and daily functioning over 12 weeks.

General Research Questions

Arizona Locations

Phoenix, Arizona, United States, 85006
Southwest Autism Research & Resource Center
Contact: Riley Stark
480-351-0567 stark@autismcenter.org
Contact: Padmaja Lakamsani
PLakamsani@autismcenter.org
Principal Investigator: Christopher Smith

California Locations

Irvine, California, United States, 92604
Amnova Clinical Research, LLC
Contact: Maggie Wang
949-358-7447 maggie@amnovaresearch.com
Contact: Jannet Guerrero
949-861-7479 jannet.guerrero@amnovaresearch.com
Principal Investigator: Gary Feldman

Orange, California, United States, 92868
Children’s Hospital of Orange County – Pediatric Subspecialty
Contact: Adrienne Moore
714-288-7456 Adrienne.Moore@choc.org
Contact: Stanley Friers
714-288-7683 Stanley.Friers@choc.org
Principal Investigator: Sailaja Golla

Sacramento, California, United States, 95817
UC Davis Mind Institute
Contact: Melissa Heys
916-703-0301 meheys@health.ucdavis.edu
Contact: Abigail Borbe
916-703-0281 amoradelhigareda@health.ucdavis.edu
Principal Investigator: Randi Hagerman

Colorado Locations

Aurora, Colorado, United States, 80045
Children’s Hospital Colorado
Contact: Nicole Tartaglia
720-777-6895 Nicole.Tartaglia@childrenscolorado.org
Principal Investigator: Nicole Tartaglia

Florida Locations

Miami, Florida, United States, 33136
University of Miami, Miller School of Medicine – Dept of Neurology
Contact: Barbara Coffey
305-243-2759 bjc134@miami.edu
Principal Investigator: Barbara Coffey

Georgia Locations

Atlanta, Georgia, United States, 30322
Emory University – The Emory Clinic – Clifton Road Contact: Robin Vinson
404-778-8533 robin.vinson@emory.edu
Contact: Nadia Ali
404-778-8613 nadia.ali@emory.edu
Principal Investigator: Amy Talboy

Illinois Locations

Chicago, Illinois, United States, 60612
Rush University Medical Center-Clinical Operation
Contact: Lorelai Konen
312-942-2815 Lorelai_Konen@rush.edu
Contact: Molly Flanagan
312-942-1876 Molly_L_Flanagan@rush.edu
Principal Investigator: Elizabeth Berry-Kravis

Maryland Locations

Baltimore, Maryland, United States, 21205
Kennedy Krieger Institute, John Hopkins School of Medicine
443-923-3850 ResearchTrials@KennedyKrieger.org
Principal Investigator: Stephanie Morris

Massachusetts Locations

Boston, Massachusetts, United States, 02115
Boston Children’s Hospital
Contact: Michelle Coughlin
857-218-3842 michelle.Coughlin@childrens.harvard.edu
Contact: Katherine Pawlowski
857-218-5472 Katherine.pawlowski@childrens.harvard.edu
Principal Investigator: Lisa Prock

Worcester, Massachusetts, United States, 01655
UMass Memorial Health
Contact: Taylor Merk
774-455-4119 Taylor.merk@umassmed.edu
Contact: Lauren Venuti
774-455-4113 Lauren.venuti@umassmed.edu
Principal Investigator: Isha Jalnapurkar

Minnesota Locations

Minneapolis, Minnesota, United States, 55414
University of Minnesota Department of Medicine
Contact: Rachel Floersch
612-626-8424 Floer013@umn.edu
Contact: Brittany Faanes
612-625-5929 Grego318@umn.edu
Principal Investigator: Amy Esler

Ohio Locations

Cincinnati, Ohio, United States, 42229
Cincinnati Children’s Hospital Medical Center
Contact: Hannah Sachs
513-803-1150 Hannah.Sachs@cchmc.org
Contact: Priya Ramesh
513-636-4433 Priya.Ramesh@cchmc.org
Principal Investigator: Rana Elmaghraby

Pennsylvania Locations

Media, Pennsylvania, United States, 19063
Suburban Research Associates
Contact: Robert Kilpatrick
610-891-9024 ext. 1128 rkilpatrick@suburbanresearch.com
Contact: Sianneh Vesslee
618-891-9024 ext. 1128
Principal Investigator: Kristen Dopf

Utah Locations

Salt Lake City, Utah, United States, 84108 Intermountain Healthcare – Park City Specialty Clinic
Contact: Peter Farr
801-587-2103 peter.farrell@hsc.utah.edu
Contact: Karina Mattson
801-587-7573 karina.mattson@hsc.utah.edu
Principal Investigator: Victoria Wilkins

Enrollment questions: